Share what’s possible
Maddy, age 21, living with Rett syndrome
*Terms and conditions apply. See FAQ for more information.
DAYBUE is the first and only FDA-approved treatment for Rett syndrome in adults and pediatric patients 2 years of age and older.
Explore what's been possible
The effectiveness and safety of DAYBUE were evaluated in the 12-week LAVENDER™ clinical study of 187 female patients aged 5 to 20 with Rett syndrome. DAYBUE was shown to significantly reduce the severity in signs and symptoms of Rett syndrome as measured by the Rett Syndrome Behaviour Questionnaire (RSBQ) compared to placebo. RSBQ assessed the following signs and symptoms: breathing, hand movements or stereotypies, repetitive behaviors, nighttime behaviors, vocalizations, facial expressions, eye gaze, and mood
The summarized caregiver perspectives shown in the gallery are unique to them and may not be the same as yours. Not all patients in the clinical study responded to treatment with DAYBUE
Because everyone with Rett syndrome is unique—with a unique set of symptoms—the response to DAYBUE may be different for each individual. Always speak with a healthcare provider to learn what to expect when starting DAYBUE, including side effects
*Families were compensated for sharing their stories.
Each patient has been on treatment with DAYBUE for at least 12 weeks. They may be also receiving other types of therapy, like occupational or speech therapy.
What are the possible side effects of DAYBUE?
Diarrhea and vomiting are the most common side effects of DAYBUE that can sometimes be severe. Other possible side effects include fever, seizure, anxiety, decreased appetite, tiredness, and the common cold.
See below for additional Important Safety Information.
Kate, age 9, living with Rett syndrome
